Gene Therapy webinar series: Episode 8 – Genetic therapies and therapy developments for ALS

13 June 2024


…TIMESLOT: Thursday 13 June 2024, 16:00 – 17:00 CET

…THEME: Genetic therapies and therapy developments for ALS

…PRESENTERS: Dr. Juan Francisco Vázquez Costa (University of Valencia, Spain)

Dr Vázquez Costa ( is MD in Neurology (2012) and PhD in motor neuron diseases (2019). Since 2013 he is devoted to the care of motor neuron disease patients and in 2020 he was granted a Juan Rodés excellence contract from the Carlos III Health Institute, to coordinate the motor neuron disease unit at Hospital la Fe. He also co-chairs the ALS Genetic Spanish consortium (ALSGESCO) and is member of the Spanish research network for rare diseases (CIBERER). This unit is a referral Spanish and European centre for the treatment and research in ALS and SMA, and participates in the European Network to Cure ALS (ENCALS) and the TRICALS consortium. Dr Vázquez Costa has participated in more than 20 research projects and in more than 30 clinical trials in both ALS and SMA, and has published more than 80 articles in indexed journals in neuromuscular diseases. He has carried out research stays at the Psychiatry department of the Universitätsklinikum in Freiburg (Germany) and at the Martinos Center for Biomedical Imaging in Boston (USA) and has collaborated and collaborates with researchers from numerous research institutes and universities. Since November 2019 he is an associate professor of neurology at the University of Valencia. 

Fore more information on the full Gene Therapy webinar series click here!

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