23 July 2024
…TIMESLOT: Tuesday 23 July 2024 – 15:00 – 16:00 CEST
…THEME: Genetic therapies and therapy developments for rare movement disorders
…PRESENTERS: Dr. Caroline Sevin (Kremlin Bicêtre Hospital, France)
Dr. Caroline Sevin is a pediatric neurologist at Kremlin Bicêtre hospital. She leads the French reference center for leukodystrophies in children at Kremlin Bicêtre hospital, France. She has long-standing interests in neurodegenerative metabolic diseases, including lysosomal, peroxysomal and mitochondrial diseases. She has a strong background in leukodystrophies, particularly Adrenoleukodystrophy, Metachromatic leukodystrophy and Krabbe disease. She’s part of international consortia for MLD and ALD. CS is PI or co-PI of several clinical trials, mostly in ALD and MLD, using innovative therapies (gene therapy, intrathecal enzyme replacement therapy, small molecules). Her research activity focuses on developing in vivo/ex vivo gene therapy and small molecules approaches for leukodystrophies.
For more information on the full Gene Therapy webinar series click here!
