The 7th Neuromuscular Translational Training School organized by EURO-NMD and hosted by the Leiden University Medical Center (LUMC) focuses on therapy development from bench to bedside with a focus on neuromuscular disorders. The Neuromuscular Translational Training School contains lectures about the current state of the art of the management of acquired and genetic neuromuscular diseases, the different steps of drug development and the tools needed for this (outcome measures, biomarkers etc). It also stresses how patients should play a role in each of these steps and teaches how to communicate research to patients and the general public during interactive workshop sessions.
Aims and objectives
- Facilitate the clinical development of therapies for NMDs
- Educate clinicians and researchers working in the NMD field on aspects relevant for translational therapy development:
- Bench to bedside research
- Regulatory system
- Clinical trials
- Outcome measures
- Patient communication
- Registries and biobanks
- Biomarkers and -omics
- Outline and showcase how networks like EURO-NMD and TREAT-NMD facilitate therapy development
- Standards of care
- Clinical trial tools
- Outcome measure development
- Interaction with stakeholders
Target audience
This programme is intended for professionals, researchers and representatives working in the field of neuromuscular diseases, including:
- Medical Doctors
- PhD students and postdoctoral researchers
- Industry delegates
- Patient representatives actively involved in the field
Programme Committee
- Annemieke Aartsma-Rus – Leiden University Medical Center, LUMC, the Netherlands
- Teresinha Evangelista – AP-HP – Hôpitaux Universitaires Pitié-Salpêtrière, Paris, France
- Andoni Urtizberea – Institut de Myologie, Paris, France
Practical information & programme
📆 2 – 5 December 2025
📍 Leiden University Medical Center, The Netherlands
📌 Click here to see the Programme!
Registration details
Registrations will open in early June.
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