International Workshop: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16-18 November 2016, Rome, Italy


Authors:

Michelangelo Mancuso, Robert McFarland, Thomas Klopstock, Michio Hirano, Consortium on Trial Readiness in Mitochondrial Myopathies


Twenty-six researchers from 10 different countries (USA, Spain, Italy, France, Germany, The Netherlands, United Kingdom, Japan, Norway and Canada) met in Rome, Italy, from 16–18 November 2016 to update current knowledge on clinical trial readiness and outcome measures for Primary Mitochondrial Myopathies (PMM). Patients’ advocacy groups delegates also attended.


Published: 8 September 2017
Journal: Neuromuscular Disorders, volume 19, issue 12, pages 1126-1137

Link: doi.org/10.1016/j.nmd.2017.08.006

The ERNs are co-funded by the
European Union (Health Programme and CEF)

EU Commission

“EURO-NMD is one of the 24 European Reference Networks (ERNs) approved by the ERN Board of Member States. The ERNs are co-funded by the European Union (Health Programme and CEF).
For more information about the ERNs and the EU health strategy,
please visit ec.europa.eu/health/ern