International Workshop: Outcome measures and clinical trial readiness in primary mitochondrial myopathies in children and adults. Consensus recommendations. 16-18 November 2016, Rome, Italy

Type of publication: An international Delphi-based consensus
Disease: Mitochondrial disease

Authors:

Michelangelo Mancuso, Robert McFarland, Thomas Klopstock, Michio Hirano, Consortium on Trial Readiness in Mitochondrial Myopathies


Twenty-six researchers from 10 different countries (USA, Spain, Italy, France, Germany, The Netherlands, United Kingdom, Japan, Norway and Canada) met in Rome, Italy, from 16–18 November 2016 to update current knowledge on clinical trial readiness and outcome measures for Primary Mitochondrial Myopathies (PMM). Patients’ advocacy groups delegates also attended.


Published: 8 September 2017
Journal: Neuromuscular Disorders, volume 19, issue 12, pages 1126-1137

Link: doi.org/10.1016/j.nmd.2017.08.006

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