Under the Horizon Europe Framework Programme, a new two-stage call for proposals for “Establishing novel approaches to improve clinical trials for rare and ultra-rare diseases” was published on 27 July, 2023. The project generated from the topic should …

The Food and Drug Administration’s (FDA) Office of Orphan Products Development (OOPD) is pleased to announce availability of funds for fiscal years (FY) 2023 – FY 2025 to support clinical trials for rare diseases and conditions. The purpose of this fun …

Child and adult neurologists from 4 European Reference Networks (MetabERN, ERN-RND, European Reference Network for Rare Neurological Diseases, ERN EpiCARE – Rare and Complex Epilepsies, and #EURONMD), Experts from the UK and Patient Avocates gathered i …

Peripheral neuropathies are a group of disorders that affect the peripheral nerves, i.e. the nerves outside the brain and spinal cord. Peripheral neuropathies caused by a series of injuries or diseases that damage the peripheral nerves can lead to a va …

Click here to register ! …TIMESLOT: October 4th 2023 at 16:00 Paris Time …THEME: Pathomechanisms of Charcot-Marie-Tooth Disease …PRESENTER: Dr. Stefano Carlo Previtali (IRCCS Ospedale San Raffaele, Italy) …BIOSKETCH: Dr. Stefano Previtali, MD, PhD, is …