Past Summer Schools

Our annual Summer School is fast becoming an estblished feature in the community’s calendar.

The courses, which are delivered by key experts in the field, are kept deliberately small to ensure a high quality, truly emersive experience for all attendees.

If you are interested in aquiring a well rounded understanding of the translational research pathway to unpin the development of your future career we recommend subscribing to our newsletter and/or follow us on Twitter @EURO_NMD to informed of programme developments and when to apply.

Below you will find information about the last two schools to provide a flavour of what can be expected.

The second Neuromuscular Translational Summer School built on the success of the first, and took place in Leiden, The Netherlands on 1st – 5th July 2019.

The five-day course which was organised and delivered in association with TREAT-NMD included an overview of the following:

  • Neuromuscular diseases and current care and management practices.
  • Bench to bedside research.
  • Challenges for rare disease therapy development and networking solutions.
  • Tools of the trade for preclinical research. · An introduction to TACT (TREAT-NMD Advisory Committee for Therapeutics) and a TACT mock review session.
  • Introduction to clinical trials.
  • How the regulatory system works.
  • The Industry perspective on drug development for rare diseases.
  • Outcome measures used in clinical trials.
  • TREAT-NMD tools for clinical trials.
  • Biomarkers.
  • PROM development.
  • Post-marketing.
  • Patient engagement.

Download our 2019 summer school programme at a glance.


We are in the process of developing our programme for the next summer school which will be held in 2020. Further information will be available in due course please regularly visit the website or monitor our twitter feed to ensure you keep up to date.

Our first ever summer school was a course was especially developed for researchers and clinicians interested in translational research.
This course addressed the following aspects as it travels along this established pathway.

  • Bench to bedside research
  • Regulatory system
  • Clinical trials
  • Outcome measures
  • Patient communication
  • Registries and biobanks
  • Biomarkers and –omics

Download our past 2018 summer school programme at a glance


Participants for our very first summer school were based at Newcastle University in the UK for the week-long school.

During their stay, they discovered how networks such as the European Reference Network EURO-NMD and TREAT-NMD work and collaborate with patients and regulators to facilitate therapy development. Aspects such as standards of care, outcome measure development, biomarkers and others were discussed and debated during the week. Attendees also found out about the various interactions that take place between key stakeholders.

Attendees discovered how the regulatory system works and also took part in a TACT style review and indepth discussion on ethical issues in clinical trials.

In addition, attendees found out about various outcome measures and gained an appreciation of the need for standardisation and training in this area. They participated in a clinical trial practicality forum as well as a patient communication workshop which focussed on patient communication which was developed especially for our school by Dutch behavioural scientists.

Attendees who completed this course now possess the knowledge of the many different aspects that are involved in translational research and also have a deeper understanding and compassion for those involved in the whole trial process from researcher to patient.

The ERNs are co-funded by the
European Union (Health Programme and CEF)

EU Commission


“EURO-NMD is one of the 24 European Reference Networks (ERNs) approved by the ERN Board of Member States. The ERNs are co-funded by the European Union (Health Programme and CEF).
For more information about the ERNs and the EU health strategy,
please visit ec.europa.eu/health/ern