This five-day summer school has been especially developed for researchers and clinicians interested in translational research.
This course addressed the following aspects as it travels along this established pathway.
- Bench to bedside research
- Regulatory system
- Clinical trials
- Outcome measures
- Patient communication
- Registries and biobanks
- Biomarkers and –omics
Participants for our very first summer school were based at Newcastle University in the UK for the week-long school.
During their stay, they discovered how networks such as the European Reference Network EURO-NMD and TREAT-NMD work and collaborate with patients and regulators to facilitate therapy development. Aspects such as standards of care, outcome measure development, biomarkers and others were discussed and debated during the week. Attendees also found out about the various interactions that take place between key stakeholders.
Attendees discovered how the regulatory system works and also took part in a TACT style review and indepth discussion on ethical issues in clinical trials.
In addition, attendees found out about various outcome measures and gained an appreciation of the need for standardisation and training in this area. They participated in a clinical trial practicality forum as well as a patient communication workshop which focussed on patient communication which was developed especially for our school by Dutch behavioural scientists.
Attendees who completed this course now possess the knowledge of the many different aspects that are involved in translational research and also have a deeper understanding and compassion for those involved in the whole trial process from researcher to patient.