Registration fee


"This course will be especially beneficial for anyone working in clinical trials."
Teresinha Evangelista - EURO-NMD

This five-day summer school has been developed for researchers and clinicians interested in translational research.
This course will address the following aspects as it travels along this established pathway.

  • Bench to bedside research
  • Regulatory system
  • Clinical trials
  • Outcome measures
  • Patient communication
  • Registries and biobanks
  • Biomarkers and –omics

Download Programme our at a Glance

Approximately 24 participants will be based at the Institute for Genetic Medicine, part of Newcastle University in the UK for the duration of the summer school.

During their stay, they will discover how networks such as the European Reference Network EURO-NMD and TREAT-NMD work and collaborate with patients and regulators to facilitate therapy development. Aspects such as standards of care, outcome measure development, biomarkers and others will be developed during the week. Attendees will also learn about the various interactions that take place between key stakeholders.

Attendees will learn how the regulatory system works, take part in a TACT style review and discuss ethical issues in clinical trials.

In addition, attendees will find out about various outcome measures and gain an appreciation of the need for standardisation and training in this area. They will participate in a clinical trial practicality forum as well as a patient communication workshop to demonstrate the results of both good and poor communication.

This comprehensive course will serve as a superb foundation for those wanting to steer their medical or research career in the direction of neuromuscular diseases whilst contacts made as a result of attending will, no doubt, prove to be invaluable.

Attendees who complete this course will not only be furnished with knowledge of the many different aspects that are involved in translational research but will also gain a deeper understanding and compassion for those involved in the whole trial process from researcher to patient.